Immunodeficiency Disease Treated Through Gene Therapy

Immunodeficiency is what affects the human body causing weakness in the immune system. This disease affects people at a young age making them vulnerable to all types of infections and complications. AIDS is the most common and dangerous immunodeficiency disease out there. These disease do not have any treatments and there hasn’t been any prior knowledge on how to control the immune system.

However, a recent study was conducted by a team of scientists from the National Institutes of Health  have developed a new way to restore immune for children with this awful disease. This is considered a breakthrough in the medical field due to the fact that there has never been any medication or treatment for these types of diseases.

The tests were conducted on eight different babies who suffer from immunodeficiency disease. This disorder is called X-linked severe combined immunodeficiency (X-SCID). The development works on gene therapy where the target is to treat the defected gene, making it stronger. After applying the test, the infants showed a better response in terms of their immune system.

The study was led by the director of NIH’s National Institute of Allergy and Infectious Diseases (NIAID) called Anthony S. Fauci, who posted the results in The New England Journal Of Medicine. He commented on his results saying, “A diagnosis of X-linked severe combined immunodeficiency can be traumatic for families. These exciting new results suggest that gene therapy may be an effective treatment option for infants with this extremely serious condition, particularly those who lack an optimal donor for stem cell transplant.”